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Diseases

Genetic and Rare Diseases Information Center (GARD)

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Methylmalonicacidemia with homocystinuria cbl d


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Treatment

Management Guidelines

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Medical Products

The medication(s) listed in the table(s) below have been approved by the Food and Drug Administration (FDA) for treatment of this condition. The FDA Office of Orphan Products Development designates "orphan products" for those that treat rare diseases affecting fewer than 200,000 Americans. The table(s) below may not be an exhaustive list of drugs or products used to treat this condition. There may be other products available that are not considered orphan products. To search for all FDA approved drugs, visit Drugs@FDA. You can find orphan products used to treat other conditions by searching the Orphan Drug Product Designation database.


Generic Name Betaine
Trade Name
(Manufacturer Name)
Cystadane
(Jazz Pharmaceuticals)
Indication
The FDA has approved this product to be used in this manner.
Treatment of homocystinuria to decrease elevated homocysteine blood levels.
More Information about this product Drug Information Portal
Medline Plus Health Information

See Disclaimer regarding information on this site. Some links on this page may take you to organizations outside of the National Institutes of Health.