Mucopolysaccharidosis type VI
Other Names for this Disease
- ARSB deficiency
- Arylsulfatase B deficiency
- ASB deficiency
- Maroteaux Lamy syndrome
- Maroteaux-Lamy disease
- ClinicalTrials.gov lists trials that are studying or have studied Mucopolysaccharidosis type VI. Click on the link to go to ClinicalTrials.gov to read descriptions of these studies.
Medical ProductsThe medication(s) listed in the table(s) below have been approved by the Food and Drug Administration (FDA) for treatment of this condition. The FDA Office of Orphan Products Development designates "orphan products" for those that treat rare diseases affecting fewer than 200,000 Americans. The table(s) below may not be an exhaustive list of drugs or products used to treat this condition. There may be other products available that are not considered orphan products. To search for all FDA approved drugs, visit Drugs@FDA. You can find orphan products used to treat other conditions by searching the Orphan Drug Product Designation database.
|Generic Name||N-acetylgalactosamine-4-sulfatase, recombinant human|
(BioMarin Pharmaceutical, Inc.)
The FDA has approved this product to be used in this manner.
|For patients with mucopolysaccharidosis VI. Galsulfase has been shown to improve walking and stair-climbing capacity.|
|More Information about this product||Drug Information Portal|