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Diseases

Genetic and Rare Diseases Information Center (GARD)

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Sickle cell disease


Other Names for this Disease

  • HbS disease
  • Hemoglobin S Disease
  • Sickle cell anemia
  • Sickling disorder due to hemoglobin S
See Disclaimer regarding information on this site. Some links on this page may take you to organizations outside of the National Institutes of Health.

Treatment

Management Guidelines

  • GeneReviews provides current, expert-authored, peer-reviewed, full-text articles describing the application of genetic testing to the diagnosis, management, and genetic counseling of patients with specific inherited conditions. Click on the link to view the article on this topic.
  • Project OrphanAnesthesia is a project whose aim is to create peer-reviewed, readily accessible guidelines for patients with rare diseases and for the anesthesiologists caring for them. The project is a collaborative effort of the German Society of Anesthesiology and Intensive Care, Orphanet, the European Society of Pediatric Anesthesia, anesthetists and rare disease experts with the aim to contribute to patient safety.

Clinical Trials & Research for this Disease

  • ClinicalTrials.gov lists trials that are studying or have studied Sickle cell disease. Click on the link to go to ClinicalTrials.gov to read descriptions of these studies.

Medical Products

The medication(s) listed in the table(s) below have been approved by the Food and Drug Administration (FDA) for treatment of this condition. The FDA Office of Orphan Products Development designates "orphan products" for those that treat rare diseases affecting fewer than 200,000 Americans. The table(s) below may not be an exhaustive list of drugs or products used to treat this condition. There may be other products available that are not considered orphan products. To search for all FDA approved drugs, visit Drugs@FDA. You can find orphan products used to treat other conditions by searching the Orphan Drug Product Designation database.


Generic Name Hydroxyurea
Trade Name
(Manufacturer Name)
Droxia®
(Bristol-Myers Squibb Pharmaceutical Research Institute)
Indication
The FDA has approved this product to be used in this manner.
To reduce the frequency of painful crises and to reduce the need for blood transfusions in adult patients with sickle cell anemia with recurrent moderate to severe painful crises (generally at least 3 during the preceding 12 months).
More Information about this product Drug Information Portal
Medline Plus Health Information

Other Names for this Disease
  • HbS disease
  • Hemoglobin S Disease
  • Sickle cell anemia
  • Sickling disorder due to hemoglobin S
See Disclaimer regarding information on this site. Some links on this page may take you to organizations outside of the National Institutes of Health.