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Hereditary antithrombin deficiency type I


Title




Other Names:
Inherited antithrombin deficiency type I; Hereditary antithrombin deficiency type 1; Inherited antithrombin deficiency classic type
This disease is grouped under:
Hereditary antithrombin deficiency

Treatment Treatment


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FDA-Approved Treatments

The medication(s) listed below have been approved by the Food and Drug Administration (FDA) as orphan products for treatment of this condition. Learn more orphan products.

  • Recombinant human antithrombin (Brand name: Atryn®) - Manufactured by GTC Biotherapeutics, Inc.
    FDA-approved indication: Prevention of peri-operative and peri-partum thromboembolic events, in hereditary antithrombin deficient patients.
    National Library of Medicine Drug Information Portal
Do you have updated information on this disease? We want to hear from you.

Research Research


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Research helps us better understand diseases and can lead to advances in diagnosis and treatment. This section provides resources to help you learn about medical research and ways to get involved.

Clinical Research Resources

  • ClinicalTrials.gov lists trials that are related to Hereditary antithrombin deficiency type I. Click on the link to go to ClinicalTrials.gov to read descriptions of these studies.

    Please note: Studies listed on the ClinicalTrials.gov website are listed for informational purposes only; being listed does not reflect an endorsement by GARD or the NIH. We strongly recommend that you talk with a trusted healthcare provider before choosing to participate in any clinical study.

Learn More Learn More


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GARD Answers GARD Answers


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Questions sent to GARD may be posted here if the information could be helpful to others. We remove all identifying information when posting a question to protect your privacy. If you do not want your question posted, please let us know.

Have a question? Contact a GARD Information Specialist.
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