The Medication(s) listed below have been approved by the Food & Drug Administration (FDA) as orphan products for treatment of this condition. There may be other products available that are not considered orphan products.

• Betaine (Brand name: Cystadane) - Manufactured by Orphan Europe SARL
  FDA-approved indication: Treatment of homocystinuria to decrease elevated homocysteine blood levels.
  National Library of Medicine Drug Information Portal Medline Plus Health Information

  Learn more about Homocystinuria due to defect in methylation cbl g