The Medication(s) listed below have been approved by the Food & Drug Administration (FDA) as orphan products for treatment of this condition. There may be other products available
that are not considered orphan products.
Asfotase alfa (Brand name: Strensiq)
- Manufactured by
Alexion Pharmaceuticals, Inc.
FDA-approved indication: For the treatment of patients with perinatal/infantile-and juvenile-onset hypophosphatasia (HPP).
National Library of Medicine Drug Information Portal