Other Names for this Disease
- PBD, ZSS
- PBD-Zellweger spectrum disorder
- Peroxisomal biogenesis disorders, Zellweger syndrome spectrum
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|Generic Name||cholic acid|
(Asklepion Pharmaceuticals, LLC)
The FDA has approved this product to be used in this manner.
|Treatment of bile acid synthesis disorders due to single enzyme defects and as adjunctive treatment of peroxisomal disorders including Zellweger spectrum disorders in patients who exhibit manifestations of liver disease, steatorrhea or complications from decreased fat soluble vitamin absorption.|
|More Information about this product||Drug Information Portal|