FDA Approved Medical Products for:


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Generic Name Sapropterin
Trade Name
(Manufacturer Name)
(Biomarin Pharmaceutical Inc.)
The FDA has approved this product to be used in this manner.
Indicated to reduce blood phenylalanine (Phe) levels in patients with hyperphenylalaninemia (HPA) due to tetrahydrobiopterin- (BH4-) responsive Phenylketonuria (PKU). Kuvan is to be used in conjunction with a Phe-restricted diet.
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