June 6, 2019
Finding treatments for rare diseases is difficult. Scientists in NCATS’ Assay Development and Screening Technology (ADST) program are collaborating with rare disease organizations to identify ways to test compounds and potential therapies for rare diseases, and speed the discovery of new treatments. Read more about ADST research and its work with alpha-1 antitrypsin deficiency, a rare cause of liver and lung disease.
Alpha-1 antitrypsin deficiency