FDA Grants Accelerated Approval to Naxitamab for High-Risk Neuroblastoma in Bone or Bone Marrow
Gaucher Disease, How a Rare Disease Provides a Window into Common Neurodegenerative Disorders
FDA Approves First Treatment for Weight Management for People with Certain Rare Genetic Conditions
Scientists Use Clues in the Human Genome to Discover New Inflammatory Syndrome
Down Syndrome Research the Intersection of Basic Science and Clinical Cohort Development
