Visit the NCATS Toolkit for Patient-Focused Therapy Development
Friday, September 8, 2017
Turner Syndrome Foundation Has A New Website!
Tuesday, September 5, 2017
HHS Establishing Pain Management Task Force/Seeks Member Nominations
Thursday, August 31, 2017
Don’t Miss the NCATS Toolkit for Patient-Focused Therapy Development Event
Thursday, August 31, 2017
2017 Million Dollar Bike Ride Pilot Grant Program
Wednesday, August 30, 2017
Funding Opportunities Now Available for the Undiagnosed Diseases Network (UDN) Phase II
Wednesday, August 30, 2017
Grant and Fellowship Opportunities from the National PKU Alliance
Wednesday, August 30, 2017
NIH Family Members Giving Back: Charlotte Phillips
Thursday, August 24, 2017
National Sickle Cell Awareness Month
Tuesday, August 22, 2017
IRDiRC Goals 2017-2027: New Rare Disease Research Goals for the Next Decade
Thursday, August 10, 2017
First In Human: Discovery Documentary on the NIH Clinical Center
Tuesday, August 8, 2017
Cause for Carey-Fineman-Ziter Syndrome Identified
Tuesday, July 11, 2017
NIH Clinical Center’s Department of Transfusion Medicine Staff Save the Life of Rare Blood Disease Patient
Thursday, July 6, 2017
Insights From Ten Years of the Hunter Outcome Survey
Thursday, July 6, 2017
FDA Approves Drug to Treat Giant Cell Arteritis
Thursday, July 6, 2017
Blood of Infants with SIDS Contains High Levels of Serotonin
Wednesday, July 5, 2017
Huntington’s Disease: Gene Editing Shows Promise in Mouse Studies
Wednesday, July 5, 2017
Autism Spectrum Disorder: Progress Toward Earlier Diagnosis
Thursday, June 15, 2017
Researchers Aim to Repurpose Former Experimental Cancer Therapy to Treat Muscular Dystrophy
Tuesday, June 13, 2017
The XVIth International Symposium on Amyloidosis
Wednesday, May 31, 2017
New Research Projects on Pearson Syndrome Underway
Tuesday, May 30, 2017
Unprecedented Trans-NCATS Collaboration Enables Rapid Advancement of Rare Lung Disease Therapy to Human Trials
Thursday, May 18, 2017
NIH, Academia and Patient Advocate Collaboration Speeds Niemann-Pick Type C1 Research
Thursday, May 18, 2017
Breathing Easier: First Treatment for Rare Lung Disease Approved
Wednesday, May 17, 2017
May is Williams Syndrome Month
Wednesday, May 3, 2017
NIH Program Strives to Turn More Lab Discoveries Into Real-World Treatments
Tuesday, May 2, 2017
Undiagnosed Day is April 29th
Wednesday, April 19, 2017
A Window Into Living With an Undiagnosed Disease
Tuesday, April 18, 2017
Regenerative Medicine: The Promise and Peril
Wednesday, April 5, 2017
Relapsing Polychondritis Study
Wednesday, April 5, 2017
NIH-Funded Scientists Deploy CRISPR to Preserve Photoreceptors in Mice
Thursday, March 16, 2017
Parkinson’s Progression Markers Initiative (PPMI)
Thursday, February 23, 2017
NCATS Seeks Applications to Repurpose Existing Drugs
Thursday, February 23, 2017
Scientists May Have Solved the Mystery of Nodding Syndrome
Thursday, February 16, 2017
International Study Suggests Nodding Syndrome Caused by Response to Parasitic Protein
Wednesday, February 15, 2017
Pearson Syndrome Research Funds Available
Tuesday, February 14, 2017
Four pivotal NIH-funded artificial pancreas research efforts begin
Tuesday, February 7, 2017
Rare and Undiagnosed Diseases: Discovery and Models of Precision Therapy
Friday, February 3, 2017
The National PKU Alliance and NORD Launch Largest-Ever Study of PKU
Wednesday, January 25, 2017
FDA Approves First Drug for Spinal Muscular Atrophy
Wednesday, January 11, 2017
Experts From NIH and The Middle East Cure Patient with Rare Tumor
Wednesday, January 11, 2017
Five NIH Grants Awarded for Collaborative Research in the Clinical Center
Wednesday, January 11, 2017
FDA Patient Representative Program
Wednesday, January 11, 2017
New Method Accurately Detects Prions in Blood
Wednesday, January 11, 2017
The Appropriateness and Cost of Thrombophilia Panel Testing: It’s Complicated
Thursday, January 5, 2017
How to Spot and Prevent Deep Vein Thrombosis
Thursday, January 5, 2017
From a Single Genetic Mutation, Secrets of ‘Boy in the Bubble’ Disease Revealed
Thursday, January 5, 2017
Combining Health Records and Genome Sequencing for Precision Medicine
Thursday, January 5, 2017
Early-Phase Trial Demonstrates Shrinkage in Pediatric Neural Tumors
Wednesday, January 4, 2017