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News Archive


ALL 2021 2020 2019

2019

October

FDA Approves Drug for Treatment of Erythropoietic Protoporphyria
Monday, October 21, 2019

2019 NIH Director's High-Risk, High-Reward Research Program Recipients Announced
Wednesday, October 2, 2019

Emerging Parasitic Disease Discovered
Wednesday, October 2, 2019

New NIH-funded Research Centers Speed and Diversify Alzheimer’s Drug Discovery
Wednesday, October 2, 2019

NIH Creates New Vector for Improved Gene Therapy in Sickle Cell Disease
Wednesday, October 2, 2019

August

Tissue Model Reveals Role of Blood-Brain Barrier in Alzheimer’s
Tuesday, August 27, 2019

Should I Be Tested for BRCA Mutations?
Tuesday, August 27, 2019

Familial Hypercholesterolemia Awareness Day - September 24th
Tuesday, August 27, 2019

July

FDA Approves Innovative Gene Therapy to Treat Pediatric Patients with Spinal Muscular Atrophy
Tuesday, July 30, 2019

June

Blood Test May Detect Myalgic Encephalomyelitis / Chronic Fatigue Syndrome
Thursday, June 13, 2019

Engineered Phages Treat Drug-Resistant Infection
Thursday, June 13, 2019

Grant Opportunity - Capacity Building for Sickle Cell Disease Surveillance
Thursday, June 6, 2019

NIH Funds Clinical Trials Using Genomics to Treat Chronic Diseases
Thursday, June 6, 2019

New Method Could Help Find Potential Treatments for Rare Diseases
Thursday, June 6, 2019

April

Anti-Inflammatory Drug Halts Strokes in Children with Rare Disease
Wednesday, April 24, 2019

NCATS-Supported Scientists Model Aging-Related Conditions in Space to Improve Human Health on Earth
Wednesday, April 24, 2019

FDA-Approved Drug Effectively Treats Rare Chronic Immune Disorder
Wednesday, April 24, 2019

Releasing an Immune System Brake Could Help Patients with Rare but Fatal Brain Infection
Wednesday, April 24, 2019

Gene Therapy Restores Immunity in Infants with Rare Immunodeficiency Disease
Wednesday, April 24, 2019

Decline in Measles Vaccination is Causing a Preventable Global Resurgence of the Disease
Wednesday, April 24, 2019

March

NIH's New Automated Tool-Set Detects Disease-Causing Genes in Undiagnosed Patients
Monday, March 4, 2019

Thoughts from the Front Lines of Rare Disease Research
Monday, March 4, 2019

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