FDA Approves Drug for Treatment of Erythropoietic Protoporphyria
Monday, October 21, 2019
2019 NIH Director's High-Risk, High-Reward Research Program Recipients Announced
Wednesday, October 2, 2019
Emerging Parasitic Disease Discovered
Wednesday, October 2, 2019
New NIH-funded Research Centers Speed and Diversify Alzheimer’s Drug Discovery
Wednesday, October 2, 2019
NIH Creates New Vector for Improved Gene Therapy in Sickle Cell Disease
Wednesday, October 2, 2019
Tissue Model Reveals Role of Blood-Brain Barrier in Alzheimer’s
Tuesday, August 27, 2019
Should I Be Tested for BRCA Mutations?
Tuesday, August 27, 2019
Familial Hypercholesterolemia Awareness Day - September 24th
Tuesday, August 27, 2019
FDA Approves Innovative Gene Therapy to Treat Pediatric Patients with Spinal Muscular Atrophy
Tuesday, July 30, 2019
Blood Test May Detect Myalgic Encephalomyelitis / Chronic Fatigue Syndrome
Thursday, June 13, 2019
Engineered Phages Treat Drug-Resistant Infection
Thursday, June 13, 2019
Grant Opportunity - Capacity Building for Sickle Cell Disease Surveillance
Thursday, June 6, 2019
NIH Funds Clinical Trials Using Genomics to Treat Chronic Diseases
Thursday, June 6, 2019
New Method Could Help Find Potential Treatments for Rare Diseases
Thursday, June 6, 2019
Anti-Inflammatory Drug Halts Strokes in Children with Rare Disease
Wednesday, April 24, 2019
NCATS-Supported Scientists Model Aging-Related Conditions in Space to Improve Human Health on Earth
Wednesday, April 24, 2019
FDA-Approved Drug Effectively Treats Rare Chronic Immune Disorder
Wednesday, April 24, 2019
Releasing an Immune System Brake Could Help Patients with Rare but Fatal Brain Infection
Wednesday, April 24, 2019
Gene Therapy Restores Immunity in Infants with Rare Immunodeficiency Disease
Wednesday, April 24, 2019
Decline in Measles Vaccination is Causing a Preventable Global Resurgence of the Disease
Wednesday, April 24, 2019
NIH's New Automated Tool-Set Detects Disease-Causing Genes in Undiagnosed Patients
Monday, March 4, 2019
Thoughts from the Front Lines of Rare Disease Research
Monday, March 4, 2019
