Medical research funding is essential for developing new diagnostic tests and treatments for rare diseases, but it can be difficult to learn about funding opportunities. The following list of resources can help medical researchers find funding sources from the National Institutes of Health (NIH) and advocacy organizations.
Where can I find NIH funding resources?
The following resources may help you search for research funding:
The NIH Office of Extramural Research offers information about research grant policies, guidelines, and funding opportunities. You can subscribe to the NIH Guide for Grants and Contracts for regular updates.
The NIH National Center for Advancing Translational Sciences offers many opportunities for funding and collaboration, including opportunities to support rare disease research.
The Center for Scientific Review (CSR) coordinates the review of NIH grant applications. CSR has a section on Applicant Resources to help you with the grant application process―from initial planning through completion.
The NIH Small Business Innovation Research and Small Business Technology Transfer programs are congressionally-mandated set-aside programs for U.S. small businesses to engage in research and development that has a strong potential for technology commercialization.
Where can I find funding resources for specific diseases?
Advocacy organizations are often an excellent resource for researchers interested in studying a specific rare disease. These groups have emerged as key partners in research by providing financial support for studies. The following organizations contacted GARD and requested to be listed as resources for research funding. Inclusion on this list is not an endorsement by GARD. Please contact GARD
if you would like to add your organization to our list.
The Alport Syndrome Foundation, the Pedersen Family, and the Kidney Foundation of Canada have partnered to provide funding for basic science and clinical research to enhance the understanding and treatment of Alport syndrome.
The Aplastic Anemia MDS International Foundation offers 2-year research grants of $30,000 per year to advance the understanding and treatment of bone marrow failure diseases, including aplastic anemia, myelodysplastic syndromes, and paroxysmal nocturnal hemoglobinuria.
The Foundation for Prader-Willi Research supports research to advance the understanding and treatment of Prader-Willi syndrome. The Foundation is particularly interested in supporting projects that will lead to new interventions to alleviate the symptoms associated with Prader-Willi syndrome.
The Prader-Willi Syndrome Association (PWSA) offers 1- to 2-year grants for a maximum of $100,000 for projects aimed at discovering and developing treatments, cures, and technologies benefiting those with Prader-Willi syndrome. PWSA supports research-based translational grants and those showing high promise for translating basic biomedical knowledge into clinical application.
The Gilead Sciences Research Scholars Program in Pulmonary Arterial Hypertension supports innovative scientific research to advance knowledge about pulmonary arterial hypertension.
The Histiocytosis Association has an annual grant program for studies investigating the cause and treatment of histiocytic disorders.
The Muscular Dystrophy Association (MDA) has a worldwide extramural research program that includes basic, clinical, and translational research efforts. MDA also helps train young physicians through Clinical Research Training Grants.
The National Ataxia Foundation funds four types of research grants for new and innovative studies that are relevant to the cause, pathogenesis, or treatment of hereditary or sporadic ataxias.
The National Marfan Foundation provides financial support for investigators studying all aspects of Marfan syndrome and related disorders.
The National MPS Society funds research that may lead to treatments for mucopolysaccharidoses and related diseases. It solicits applications for innovative research projects that involve basic research, translational studies, and clinical research.
The National Organization for Rare Disorders Research Grant Program provides seed grants to academic scientists for translational or clinical studies related to development of potential new diagnostics or treatments for rare diseases.
NephCure Kidney International supports scientists pursuing research designed to improve the understanding of nephrotic syndrome diseases.
The Progeria Research Foundation offers grants to support research aimed at developing effective treatments for Hutchinson-Gilford progeria syndrome and related disorders.
The Pulmonary Hypertension Association Research Program provides grants to researchers seeking to better understand pulmonary hypertension. The program supports research projects ranging from early exploratory work to projects that facilitate mentorships that will ensure a future of innovative investigators.
The United Mitochondrial Disease Foundation promotes research and education for the diagnosis, treatment, and cure of mitochondrial disorders. The Foundation awards more than $1 million per year in grants to scientists conducting basic research on mitochondrial disorders, and for clinical studies focusing on diagnosis and treatment.
The Vasculitis Foundation Research Grant Program provides 1- or 2-year seed grants to support pilot studies researching the etiology, epidemiology, diagnosis, and treatment of people with vasculitis.
Last updated: 6/24/2016